Parcourir par sujet "Duchenne muscular dystrophies"
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Modeling the off-target effects of CRISPR-Cas9 experiments for the treatment of Duchenne Muscular Dystrophy
(2022)Duchenne Muscular Dystrophy (DMD) is a neuromuscular disorder caused by the absence of the dystrophin protein. If left untreated, it causes movement problems at the age of 10-12 years, and death occurs in the 20-30 years ...